A model of inherited retinal channelopathy with a nonviral base editing of KCNJ13 mutation

In this episode, Bikash Pattnaik and colleagues explain that their study encompasses the application of genomic medicine to treat monogenic retinal degeneration using base editing gene therapy delivered through novel nonviral platform.

• #science_technology
• #jci_authors_take
• #video_abstract
• #ophthalmology
• #gene_therapy
• #ion_channels
• #nanotechnology