NACFC 2023 | W29: Accelerating Progress Along the Path to a Cure

Cystic Fibrosis Foundation
Cystic Fibrosis Foundation
70 بار بازدید - 8 ماه پیش - This session features pre-clinical research
This session features pre-clinical research focused on developing therapies for cystic fibrosis. Topics include cystic fibrosis transmembrane conductance regulator (CFTR) super-exon approaches, anti-CD20 treatment to attenuate immune responses associated with gene transfer, autologous stem cell gene therapy, CFTR mRNA delivery via nanoparticles, and picovectors delivering nonsense suppressor tRNA. These studies highlight important work done to advance the Path to a Cure mission to restore CFTR activity for all people with CF.

Originally recorded November 3, 2023.
8 ماه پیش در تاریخ 1402/08/29 منتشر شده است.
70 بـار بازدید شده
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