UCLA Stem Cell Researchers Announce Gene Therapy Cure for 18 ‘Bubble Baby’ Patients

On November 18, 2014, researchers at UCLA announced that they had cured 18 children who were born with the so-called Bubble Baby disease, a genetic disorder that leaves the young sufferers without a working immune system, putting them at risk of death from infections, even the common cold.

A team led by Dr. Donald Kohn, a stem cell researcher at the university’s Eli and Edythe Broad Center of Regenerative Medicine and Stem Cell Research in Los Angeles, developed the breakthrough that cured 18 children who had adenosine deaminase (ADA)-deficient severe combined immunodeficiency (SCID).

Read more: https://www.stemcell.ucla.edu/news/st...

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