CRISPR gene-editing treatment for sickle cell disease explained

Casgevy is the first FDA-approved medical treatment based on CRISPR gene-editing technology. Barely a decade after CRISPR gene-editing was discovered, the first medical treatment based on this revolutionary technology was approved by the U.S. Food and Drug Administration and now people with sickle cell disease, a painful, life-limiting, inherited blood disorder, have the potential for a cure.
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• #molecular
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