Spinal Muscular Atrophy

ASGCT
ASGCT
40.8 هزار بار بازدید - 6 سال پیش - Gene therapy is a fitting
Gene therapy is a fitting approach for diseases caused by a single gene mutation, like SMA. It targets the cause of disease by delivering a fully functioning copy of the gene into motor neuron cells. Let’s learn more about how it works.

The subtitling of these videos was funded in part by a donation from Pfizer, Inc.
6 سال پیش در تاریخ 1397/11/12 منتشر شده است.
40,800 بـار بازدید شده
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